Der Ruf nach Pay-for-Performance-Erstattungsmodellen für neuartige und hochpreisige Gentherapien wurde in den vergangenen Jahren immer lauter. Schon vor einigen Jahren prognostizierte der unparteiische Vorsitzende des Gemeinsamen Bundesausschusses, Josef Hecken, das entsprechende Verträge das Finanzierungsmodell der Zukunft sein werden – „zumindest bei ganz teuren Gentherapien, einfach auch, um einen indikations- und diagnosegerechten Einsatz dieser Medikamente in der Fläche zu gewährleisten“.
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